Development of orphan drugs for rare disease
Han-Wook Yoo
Received 2023 Apr 3     Accepted 2023 Jun 28     Published online 2023 Jun 28     DOI: https://doi.org/10.3345/cep.2023.00535    
[Accepted]
Citations to this article as recorded by Crossref logo
Drug Repurposing and Lysosomal Storage Disorders: A Trick to Treat
Bruno Hay Mele, Federica Rossetti, Maria Vittoria Cubellis, Maria Monticelli, Giuseppina Andreotti
Genes.2024; 15(3): 290.     CrossRef
Building advocacy into research
James F. Amatruda
Disease Models & Mechanisms.2023;[Epub]     CrossRef